Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.

New research shows it’s possible to edit the DNA of human embryos with more precision. But scientists warn it’s still not ...

A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child with a rare genetic disorder. Unlike earlier ...

Researchers discovered the secret checkpoints that keep CRISPR precise, revealing how the tool shifts from inactive to active without misfiring. The insight could transform gene therapy, making ...

The gene editing tool known as CRISPR-Cas9 is changing what's possible for treating a wide range of diseases caused by genetic mutations. But so far, attempts to use the technology to address ...

This new technology could one day significantly expand the market for gene-editing biotechs.

The CRISPR gene editing system holds tremendous promise. It has already revolutionized biomedical research by making gene editing a straightforward process. It involves using a guide RNA molecule that ...

Researchers are investigating the potential of CRISPR in relation to Down syndrome.

A team of researchers led by Luigi Naldini at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget) has developed a new strategy to significantly improve the precision and safety of ...

One has FDA approval and revenue; the other is pre-commercial but debt-free. Both face distinct risks that could reshape your ...

People living with hereditary angioedema, a rare genetic condition that triggers unpredictable and sometimes life-threatening ...